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Cat No. | Product Name | Synonyms | Targets |
---|---|---|---|
T7117 | Sapropterin dihydrochloride | Sapropterin Hydrochloride , 6R-Tetrahydro-L-biopterin dihydrochloride , 6R-BH4 dihydrochloride | Hydroxylase |
Sapropterin dihydrochloride (6R-BH4 dihydrochloride) is phenylalanine hydroxylase agonist that is approved for the treatment of BH4 responsive PKU. |